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Rare Diseases: Drugs

Question for Department of Health and Social Care

UIN 202780, tabled on 16 October 2023

To ask the Secretary of State for Health and Social Care, how many highly specialised technology evaluations of medicines for very rare diseases conducted by the National Institute for Health and Care Excellence resulted in (a) a positive recommendation, (b) an optimised recommendation, (c) a recommendation for managed access, (d) a negative recommendation and (e) termination in each financial year since 2018-19.

Answered on

20 October 2023

The following table shows a breakdown of technologies appraised through the National Institute for Health and Care Excellence’s highly specialised technology process by financial year from 2018/19:

Financial Year

2018/19

2019/20

2020/21

2021/22

2022/23

Total

Recommended

1

4

2

4

4

15

Optimised

0

0

0

0

1

1

Not recommended

0

0

0

0

0

0

Total

1

4

2

4

5

16

Terminated

0

0

0

0

0

0